Watch The Genetics of Hope

Follow the families, patients, and scientists who rallied together to create the first approved treatment for a rare genetic disease called Spinal Muscular Atrophy (SMA). The SMA community is a model community where a collaborative approach to problem-solving yielded a breakthrough in medicine, accelerating the development of treatments that improve the lives of people with genetic diseases.

The Genetics of Hope is a 2020 documentary with a runtime of 28 minutes.